How this gene therapy drug earned it’s $2.1 million price tag
Swiss drugmaker Novartis recently launched a lottery-style program to allocate free doses of Zolgensma, its groundbreaking treatment for children with spinal muscular atrophy (SMA), to patients in countries that haven't approved the drug. But with a $2.1 million price tag, Zolgensma is inaccessible to some patients even where it has been approved. The prohibitive cost has been a source of criticism since the drug was approved. In a letter to the U.S. Food and Drug Administration's (FDA) Acting Commissioner last August, five U.S. senators, including presidential...